The current state of long-acting growth hormone preparations for growth hormone therapy.
Department
Neuroendocrinology
Document Type
Article
Abstract
PURPOSE OF REVIEW: To discuss the rationale of developing long-acting growth hormone (LAGH) preparations, to describe the technologies designed to prolong GH action, and to address key issues regarding efficacy, safety, and monitoring while on treatment.
REVIEW FINDINGS: Recombinant human GH is currently approved for daily use and has been shown to restore longitudinal growth, and improve body composition with relatively few side-effects in children and adults with GH deficiency, respectively. However, daily injections can be inconvenient, painful and distressing for some patients, resulting in decreased adherence and efficacy. Over a dozen pharmaceutical companies have designed LAGH preparations that are at various stages of development using a number of different methods to prolong GH action.
SUMMARY: LAGH will represent an advancement over daily recombinant human GH injections because of fewer injections that may offer increased acceptance, tolerability, and therapeutic flexibility to patients that potentially can improve treatment outcomes. However, given the unphysiological profile of LAGH preparations, long-term surveillance of efficacy and safety are needed. This review summarizes recent developments of LAGH preparations, and highlights the importance of long-term surveillance registries to assess for efficacy and safety that will be essential for understanding the impact of prolonged exposure to these compounds.
Medical Subject Headings
Adult; Body Composition; Body Height; Child; Delayed-Action Preparations; Human Growth Hormone; Humans; Injections; Technology, Pharmaceutical; Treatment Outcome
Publication Date
8-1-2018
Publication Title
Curr Opin Endocrinol Diabetes Obes
ISSN
1752-2978
Volume
25
Issue
4
First Page
267
Last Page
273
PubMed ID
29746309
Digital Object Identifier (DOI)
10.1097/MED.0000000000000416
Recommended Citation
Yuen, Kevin C J; Miller, Bradley S; and Biller, Beverly M K, "The current state of long-acting growth hormone preparations for growth hormone therapy." (2018). Neurology. 311.
https://scholar.barrowneuro.org/neurology/311