A validated LC-MS/MS method for determination of neuro-pharmacokinetic behavior of niraparib in brain tumor patients.
Document Type
Article
Abstract
Niraparib is a potent and orally bioavailable inhibitor of poly (ADP-ribose) polymerase (PARP) with high specificity for isoforms 1 and 2. It has been approved by the U.S. Food and Drug Administration for ovarian cancer maintenance therapy and is currently under development for various cancers, including glioblastoma. To assess central nervous system (CNS) penetration of niraparib in glioblastoma patients, a novel bioanalytical method was developed to measure total and unbound niraparib levels in human brain tumor tissue and cerebrospinal fluid (CSF). The method was validated using plasma as a surrogate matrix over the concentration range of 1-10,000 nM on an LC-MS/MS system. The MS/MS detection was conducted in positive electrospray ionization mode, while chromatography was performed using a Kinetex™ PS C18 column with a total 3.5-minute gradient elution run time. The maximum coefficient of variation for both intra- and inter-day precision was 10.6%, with accuracy ranging from 92.8% - 118.5% across all matrices. Niraparib was stable in human brain homogenate for at least 6 hours at room temperature (RT) and 32 days at -20°C, as well as in stock and working solutions for at least 21 hours (RT) and 278 days (4°C). Equilibrium dialysis experiments revealed the fractions unbound of 0.05 and 0.16 for niraparib in human brain and plasma, respectively. The validated method is currently employed to assess niraparib levels in human glioblastoma tissue, CSF, and plasma in an ongoing trial on newly diagnosed glioblastoma and recurrent IDH1/2(+) ATRX mutant glioma patients (NCT05076513). Initial results of calculated total (K
Keywords
Humans, Piperidines, Indazoles, Tandem Mass Spectrometry, Brain Neoplasms, Poly(ADP-ribose) Polymerase Inhibitors, Chromatography, Liquid, Glioblastoma, Reproducibility of Results, Brain, Sulfonamides, Liquid Chromatography-Mass Spectrometry
Medical Subject Headings
Humans; Piperidines; Indazoles; Tandem Mass Spectrometry; Brain Neoplasms; Poly(ADP-ribose) Polymerase Inhibitors; Chromatography, Liquid; Glioblastoma; Reproducibility of Results; Brain; Sulfonamides; Liquid Chromatography-Mass Spectrometry
Publication Date
8-1-2024
Publication Title
Journal of pharmaceutical and biomedical analysis
ISSN
1873-264X
Volume
245
First Page
116150
Last Page
116150
PubMed ID
38657366
Digital Object Identifier (DOI)
10.1016/j.jpba.2024.116150
Recommended Citation
Knight, William; Margaryan, Tigran; Sanai, Nader; and Tovmasyan, Artak, "A validated LC-MS/MS method for determination of neuro-pharmacokinetic behavior of niraparib in brain tumor patients." (2024). Translational Neuroscience. 2393.
https://scholar.barrowneuro.org/neurobiology/2393